Researchers identified a molecular pathway that can limit muscle repair, a finding that may guide future muscular dystrophy treatments.
Roche has decided to stop developing satralizumab for bone health in Duchenne muscular dystrophy, the company announced.
After years of focusing on her large family, and three sons with Duchenne MD, columnist Betty Vertin is eager to reconnect with friends.
After following the Olympics, columnist Robin Stemple envisions a future with new treatments and even a cure for FSHD.
Dosing has begun in a Phase 2 clinical trial testing the experimental oral therapy SAT-3247 in boys with Duchenne muscular ...
Columnist Shalom Lim has discovered that a personal sense of belonging is built through simple presence. Art can help foster ...
Guest writer Matthew Busch says that, despite the setbacks and surgeries he's endured, he's now thriving in life with Duchenne MD.
Lasting gains in swallowing ability have been reported for four people with oculopharyngeal muscular dystrophy given gene therapy in a trial.
Columnist Patrick Moeschen turns to classic writers and poets to express how he is choosing hope in life with limb-girdle muscular dystrophy.
Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...
A young man with Duchenne muscular dystrophy (DMD) who received the one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) has died due to acute liver failure. In a statement, the ...